Dan Williams discusses gene silencing in this important piece for Drug Target ReviewDr Dan WilliamsApr 151 min readGene silencing: a step forward for rare disease therapy - Drug Target Review
Dan Williams contributes to a major article for Inside Precision Medicine, in which several US families with a child living with H-ABC discuss their journey to a diagnosis
Dan Williams welcomes news that NICE has raised the cost-effectiveness threshold for ultra-rare disease drugs
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