British biotech firm secures FDA rare paediatric disease designation
British biotech firm secures FDA rare paediatric disease designation in bid to develop world’s first treatment for incurable, deadly disease
British biotech firm secures FDA rare paediatric disease designation
Children with undiagnosed conditions urged to get checked for rare, incurable and deadly disease
We were delighted to welcome Sky News to Oxfordshire in November
The powerful story of Frankie Sheridan-Hill, aged seven, featured on ITV
SynaptixBio agrees US children’s hospital deal to develop world’s first treatment for deadly disease
‘Time running out’ in teen girl’s battle with TUBB4a leukodystrophy
Thousands of patients could have rare life-threatening diseases without knowing it, experts warn
Mum diagnoses daughter's rare life-threatening disease
New biotech firm launched to develop ‘revolutionary’ treatment for one of world’s rarest diseases