British biotech firm secures FDA rare paediatric disease designation
British biotech firm secures FDA rare paediatric disease designation in bid to develop world’s first treatment for incurable, deadly disease
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- Jan 8
Children with undiagnosed conditions urged to get checked for rare, incurable and deadly disease
Children with undiagnosed conditions urged to get checked for rare, incurable and deadly disease
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- Nov 12, 2022
We were delighted to welcome Sky News to Oxfordshire in November
We were delighted to welcome Sky News to Oxfordshire in November
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- Nov 2, 2022
The powerful story of Frankie Sheridan-Hill, aged seven, featured on ITV
The powerful story of Frankie Sheridan-Hill, aged seven, featured on ITV
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- Oct 17, 2022
SynaptixBio agrees US children’s hospital deal to develop world’s first treatment for deadly disease
Biotech firm enters into a pioneering new licence agreement in bid to develop world’s first treatment for deadly disease
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- Sep 8, 2022
‘Time running out’ in teen girl’s battle with TUBB4a leukodystrophy
‘Time running out’ in teen girl’s battle with TUBB4a leukodystrophy
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- Feb 7, 2022
Thousands of patients could have rare life-threatening diseases without knowing it, experts warn
Thousands of patients could unknowingly suffer with a rare life-threatening disease, experts have warned. TUBB4a leukodystrophy - an...
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- Oct 1, 2021
Mum diagnoses daughter's rare life-threatening disease
Mum diagnoses daughter's rare life-threatening disease
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- Aug 18, 2021
New biotech firm launched to develop ‘revolutionary’ treatment for one of world’s rarest diseases
New biotech firm launched to develop ‘revolutionary’ new treatment for one of world’s rarest neurodegenerative diseases
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